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Orphan Medical Incorporated Company Profile

01:12 EDT 21st September 2017 | BioPortfolio

Orphan Medical Incorporated is a development stage company, was formed to acquire, develop and market products of high medical value intended to address inadequately treated or uncommon diseases of well-defined patient populationstreated by health care specialists. A drug has high medical value if it offers a major improvement in the safety or efficacy of patient treatment and has no substantially equivalent substitute.

Location

13911 Ridgedale Drive, Suite 475
Minnetonka
MN
55305
United States of America

Contact

Phone: 612 513 6900


News Articles [1452 Associated News Articles listed on BioPortfolio]

Study Shows Magnitude of Benefit Scale Can Be Used to Grade Orphan Drugs

NewsThis study used the ESMO-MCBS tool to determine how orphan and non-orphan drugs performed according to its established threshold for meaningful benefit.

ESMO 2017: Study Shows Magnitude of Benefit Scale Can Be Used to Grade Orphan Drugs

NewsThis study used the ESMO-MCBS tool to determine how orphan and non-orphan drugs performed according to its established threshold for meaningful benefit.

FDA outlines efforts to reduce orphan drug designation backlog

David SalazarThe agency has outlined its Orphan Drug Modernization plan, which it said is part of a larger effort called the Medical Innovation Development plan modernize and make efficient the FDA&rs...

Orphan Drug Pricing Heading To Negotiating Table in US?

ICER is launching an initiative to adapt its value assessment approach to orphan and ultra-orphan drugs, including a possible consideration...   

Chondrial Announces FDA Orphan Drug Designation for CTI-1601, a Novel Investigational ...

Orphan drug designation is granted by the FDA Office of Orphan Products Development to drugs being developed for safe and effective treatment of diseases that affect fewer Read more...

Jupiter Orphan Therapeutics Receives Orphan Drug Designation for its Trans-Resveratrol Product ...

JUPITER, Fla., Aug. 22, 2017/PRNewswire/ -- Jupiter Orphan Therapeutics, Inc. ("JOT"), Jupiter, FL, today announced that it has received notification from the US Read more...

EMA grants orphan drug status to RDD Pharma's RDD─0315 to treat fecal incontinence in patients with spinal cord injury

RDD Pharma, a leader in developing treatments for anorectal disorders, has announced the European Medicines Agency's Committee for Orphan Medicinal Products has granted orphan designation for RDD─03...

Friedreich's Ataxia Treatment Receives Orphan Drug Designation

NewsJupiter Orphan Therapeutics receives Orphan Drug designation for its trans-resveratrol product Jotrol for treatment of Friedreich's Ataxia. It is a rare inherited disease that causes damage to the...

PubMed Articles [2816 Associated PubMed Articles listed on BioPortfolio]

Affordable orphan drugs: A role for not-for-profit organisations.

The success of the Regulation on Orphan Medicinal Products in the European Union is evidenced by the 127 orphan drugs that have had market authorisation since 2000. However the incentives aimed to sti...

Direct-to-Consumer Genetic Testing and Orphan Drug Development.

Since the introduction of the Orphan Drug Act (ODA) in 1983, orphan drug approvals in the United States have jumped from

Prioritizing Rare Diseases.

Measuring societal preferences for rarity has been proposed to determine whether paying premium prices for orphan drugs is acceptable.

Pharmacology and drug development in rare diseases: the attractiveness and expertise of the French medical pharmacology.

Developing drugs for rare disease can be challenging due to specific rare disease characteristics. The French Medical Pharmacology is structured and positioned to play a major role in Orphan Drug Rese...

Retinoic acid-related orphan receptor alpha (RORA) variants and risk of breast cancer.

Breast cancer is the most common type of cancer and the second leading cause of cancer death in females. Despite numerous studies in this field, the etiology and clinical behavior of breast tumors hav...

Clinical Trials [1396 Associated Clinical Trials listed on BioPortfolio]

Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A

This is an open, Phase I / II clinical trial to evaluate the safety and efficacy of a hematopoietic gene therapy procedure with an orphan drug consisting of a lentiviral vector carrying th...

A Safety and Pharmakokinetic Study of A4250 Alone or in Combination With A3384

The primary objectives of the study are to evaluate the safety, tolerability and pharmacokinetics of A4250 after single or multiple oral doses in healthy subjects. In addition, will evalua...

Study of Genetic Polymorphisms of Drug Transporters and Orphan Nuclear Receptors on Treatment Effects of Irinotecan

From 100 colorectal cancer patients being treated with FOLFIRI regimen or any kind of irinotecan containing regimen, blood samples for irinotecan and its metabolites levels and genotypes r...

The LD Lync Study - Natural History Study of Genetic Lipodystrophy Syndromes

Genetic lipodystrophy syndromes are extremely rare, orphan diseases with overall estimated prevalence of less than 2,000 in the United States. These rare disorders characterized by selecti...

An Open Label, Single-dose, Single Period ADME Study of A4250 in Healthy Subjects

The primary objectives of the study are to assess the mass balance recovery after a single dose of carbon-14 [14C]-A4250 as a capsule and to provide plasma, urine and faecal samples for me...

Companies [1280 Associated Companies listed on BioPortfolio]

Orphan Medical Incorporated

Orphan Medical Incorporated is a development stage company, was formed to acquire, develop and market products of high medical value intended to address inadequately treated or uncommon diseases of we...

Insmed Incorporated

Insmed Incorporated is a biopharmaceutical company dedicated to improving the lives of patients battling serious lung diseases. Insmed is focused on the development and commercial...

Orphan Europe (UK) Ltd.

Orphan Europe was started with the objective of providing orphan drugs to patients afflicted by rare disorders.Over the years an information network has been established to increase the awareness abou...

PRAECIS PHARMACEUTICALS INCORPORATED

PRAECIS PHARMACEUTICALS INCORPORATED is a biopharmaceutical company focused on the discovery and development of novel compounds to address unmet medical needs or improve existing therapies.PRAECIS has...

Santhera Pharmaceuticals Holding Ltd

Santhera Pharmaceuticals is a Swiss biopharmaceutical company focusing on the discovery, development and marketing of small molecule pharmaceutical products for the treatment of neuromuscular diseases...

More Information about "Orphan Medical Incorporated" on BioPortfolio

We have published hundreds of Orphan Medical Incorporated news stories on BioPortfolio along with dozens of Orphan Medical Incorporated Clinical Trials and PubMed Articles about Orphan Medical Incorporated for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Orphan Medical Incorporated Companies in our database. You can also find out about relevant Orphan Medical Incorporated Drugs and Medications on this site too.

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