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Cure Duchenne Company Profile

13:08 EST 8th December 2016 | BioPortfolio

Cure Duchenne, a national nonprofit organization located in Newport Beach, Calif., is gaining international attention for its efforts to raise funds and awareness for Duchenne – a devastating and lethal muscle disease in children. One in every 3,500 male births results in a child being afflicted with the disease. Nearly 20,000 boys are living with the disease in the United States alone, and many will not survive their teenage years. The disorder knows no ethnic or social boundaries.


News Articles [720 Associated News Articles listed on BioPortfolio]

FDA greenlights Sarepta Therapeutics’ milestone treatment for Duchenne muscular dystrophy

Exondys 51 doesn’t cure Duchenne muscular dystrophy and will only help a minority of patients.

Sarepta Preps For Sales As Insurers Unlikely To Deny Duchenne Drug

Kathryn Wagner treats boys with Duchenne muscular dystrophy, a rare and fatal genetic disease. She thinks the first drug ever approved to treat Duchenne is “horrendously expensive,” and sh...

JAR of Hope's Much Anticipated HBOT Study a Reality -- Pre-Clinical Trial Underway at the ...

Foundation Steadfast in Its Mission to Cure Duchenne Muscular Dystrophy Partners With the University of Minnesota to Prove Efficacy of Oxygen Treatment by Utilizing a Read more...

Duchenne drug gets FDA approval in “unprecedented” ruling

The FDA has gone against the advice of its own staff to approve the first treatment of Duchenne muscular dystrophy (DMS) in Sarepta’s Exondys 51. read more

After New Data, FDA Bucks Advisory Panel, Approves Sarepta’s Duchenne Drug

[Updated 9/19/16, 12:42 p.m. See below.] In a decision that could have myriad implications for both the pharmaceutical industry and patients with Duchenne muscular dystrophy, the FDA today approved a ...

Marathon seeks approval for Duchenne treatment

A new-drug application for deflazacort as a treatment for Duchenne muscular dystrophy has been submitted to the FDA by Marath -More- 

Jett Foundation to "Shine a Light on Duchenne" on Duchenne Awareness Day 2016 in Cambridge, Mass.

KINGSTON, Mass., Sept. 6, 2016 /PRNewswire-USNewswire/ -- Today, Jett Foundation, a 501(c)(3) committed to meeting the unmet needs of patients and families affected by Duchenne muscular dystrophy (DMD...

Pharmalot, Pharmalittle: Duchenne drug rejected in US is available in England

The National Health Service in England agreed to cover a Duchenne muscular dystrophy drug made by PTC Therapeutics.

PubMed Articles [310 Associated PubMed Articles listed on BioPortfolio]

Parental Reflections on the Diagnostic Process for Duchenne Muscular Dystrophy: A Qualitative Study.

Duchenne muscular dystrophy (DMD) is a rare neuromuscular disease with no known cure. We sought to update over 30 years of research reporting on the diagnostic delays in DMD.

Towards a scalable HIV cure research agenda: the role of co-infections.

The development of a cure is among the foremost contemporary priorities in the field of HIV research. The science that underpins a potential HIV cure should be generalisable to the many millions of pe...

Expression of positive emotions differs in illness and recovery in anorexia nervosa.

People with Anorexia Nervosa (AN) display reduced facial expression of emotions. This study investigated the expression of positive affect in response to a film, examining Duchenne and non-Duchenne sm...

Residual-based model diagnosis methods for mixture cure models.

Model diagnosis, an important issue in statistical modeling, has not yet been addressed adequately for cure models. We focus on mixture cure models in this work and propose some residual-based methods...

Economic Evaluation in Duchenne Muscular Dystrophy: Model Frameworks for Cost-Effectiveness Analysis.

Several treatments are on the horizon for Duchenne muscular dystrophy (DMD), a terminal orphan disease. In many jurisdictions, decisions regarding pricing and reimbursement of these health technologie...

Clinical Trials [480 Associated Clinical Trials listed on BioPortfolio]

Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2

Duchenne Muscular Dystrophy (DMD) is a X-linked genetic disorder primarily affecting males, resulting in an absence of dystrophin which ultimately leads to progressive muscle degeneration....

Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy

The purpose of this study is to determine if ACE-031 is safe and well-tolerated in children with Duchenne Muscular Dystrophy (DMD) and to select the optimal doses of ACE-031 in terms of sa...

A Study of TAS-205 for Duchenne Muscular Dystrophy

The objective of this study is to evaluate the efficacy after 24-week repeated oral doses of TAS-205 in patients with Duchenne Muscular Dystrophy (DMD) in an exploratory manner.

Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy

The purpose of this research study is to understand the walking patterns, strength and function changes of boys with Duchenne muscular dystrophy on/off corticosteroids to determine the bes...

HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne)

The safety objective of the HOPE-Duchenne trial will be to investigate the safety and tolerability of CAP-1002 administered by multi-vessel intracoronary infusion in subjects with cardiomy...

Companies [242 Associated Companies listed on BioPortfolio]

Cure Duchenne

Cure Duchenne, a national nonprofit organization located in Newport Beach, Calif., is gaining international attention for its efforts to raise funds and awareness for Duchenne â...

Jett Foundation

Based in Kingston, MA the Jett Foundation is a non-profit organization dedicated to increasing worldwide awareness of Duchenne Muscular Dystrophy with the purpose of raising and a...

Standup for the Cure

Standup for the Cure is a Non-Profit Corporation formed in 2012 which raised more than $60,000 at its inaugural May event for the Orange County Affiliate of Susan G. Komen For The...

Accelerated Cure Project

Accelerated Cure Project for Multiple Sclerosis, www.acceleratedcure.org, is a national nonprofit organization dedicated to curing Multiple Sclerosis (MS) by determining its cause...

P‐Cure Ltd.

P‐Cure develops advanced solutions that help bring proton therapy to routine clinical practice. The P-Cure system provides an integrated solution with volumetric imaging, pat...

More Information about "Cure Duchenne" on BioPortfolio

We have published hundreds of Cure Duchenne news stories on BioPortfolio along with dozens of Cure Duchenne Clinical Trials and PubMed Articles about Cure Duchenne for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Cure Duchenne Companies in our database. You can also find out about relevant Cure Duchenne Drugs and Medications on this site too.

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