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Cure Duchenne Company Profile

10:12 EST 22nd February 2017 | BioPortfolio

Cure Duchenne, a national nonprofit organization located in Newport Beach, Calif., is gaining international attention for its efforts to raise funds and awareness for Duchenne – a devastating and lethal muscle disease in children. One in every 3,500 male births results in a child being afflicted with the disease. Nearly 20,000 boys are living with the disease in the United States alone, and many will not survive their teenage years. The disorder knows no ethnic or social boundaries.


News Articles [709 Associated News Articles listed on BioPortfolio]

FDA greenlights Sarepta Therapeutics’ milestone treatment for Duchenne muscular dystrophy

Exondys 51 doesn’t cure Duchenne muscular dystrophy and will only help a minority of patients.

FDA Clears Marathon Drug Deflazacort for All Genetic Forms of DMD

FDA approved Marathon Therapeutics’s oral steroid drug, EMFLAZA™ (deflazacort), for treating Duchenne muscular dystrophy in patients aged five years and over, irrespective of the underlying geneti...

CureDuchenne Applauds the FDA Approval of Marathon’s EMFLAZA (deflazacort) for the Treatment of Duchenne Muscular Dystrophy

EMFLAZA is the First Drug in the U.S. Approved for Use by Patients Age Five and Older with Duchenne Regardless of Genetic Mutation CureDuchenne applauds the U.S. Food a...

Sarepta Preps For Sales As Insurers Unlikely To Deny Duchenne Drug

Kathryn Wagner treats boys with Duchenne muscular dystrophy, a rare and fatal genetic disease. She thinks the first drug ever approved to treat Duchenne is “horrendously expensive,” and sh...

Duchenne drug gets FDA approval in “unprecedented” ruling

The FDA has gone against the advice of its own staff to approve the first treatment of Duchenne muscular dystrophy (DMS) in Sarepta’s Exondys 51. read more

After New Data, FDA Bucks Advisory Panel, Approves Sarepta’s Duchenne Drug

[Updated 9/19/16, 12:42 p.m. See below.] In a decision that could have myriad implications for both the pharmaceutical industry and patients with Duchenne muscular dystrophy, the FDA today approved a ...

PPMD awards $600,000 to NJIT and Talem for Duchenne muscular dystrophy exoskeleton

(New Jersey Institute of Technology) Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), today announced a $600,000 gran...

BioMarin Release: Biotech Transfers Duchenne Natural History Database To CureDuchenneTo Improve Knowledge Of Duchenne Patients And Improve Clinical Outcomes

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PubMed Articles [279 Associated PubMed Articles listed on BioPortfolio]

Parental Reflections on the Diagnostic Process for Duchenne Muscular Dystrophy: A Qualitative Study.

Duchenne muscular dystrophy (DMD) is a rare neuromuscular disease with no known cure. We sought to update over 30 years of research reporting on the diagnostic delays in DMD.

Expression of positive emotions differs in illness and recovery in anorexia nervosa.

People with Anorexia Nervosa (AN) display reduced facial expression of emotions. This study investigated the expression of positive affect in response to a film, examining Duchenne and non-Duchenne sm...

Residual-based model diagnosis methods for mixture cure models.

Model diagnosis, an important issue in statistical modeling, has not yet been addressed adequately for cure models. We focus on mixture cure models in this work and propose some residual-based methods...

Economic Evaluation in Duchenne Muscular Dystrophy: Model Frameworks for Cost-Effectiveness Analysis.

Several treatments are on the horizon for Duchenne muscular dystrophy (DMD), a terminal orphan disease. In many jurisdictions, decisions regarding pricing and reimbursement of these health technologie...

New Survival Target for Duchenne Muscular Dystrophy.

We report a patient with a typical phenotype and clinical history of Duchenne muscular dystrophy who is currently 53 years old. Because of improvements in cardiopulmonary care, there has been a great ...

Clinical Trials [492 Associated Clinical Trials listed on BioPortfolio]

Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2

Duchenne Muscular Dystrophy (DMD) is a X-linked genetic disorder primarily affecting males, resulting in an absence of dystrophin which ultimately leads to progressive muscle degeneration....

Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy

The purpose of this study is to determine if ACE-031 is safe and well-tolerated in children with Duchenne Muscular Dystrophy (DMD) and to select the optimal doses of ACE-031 in terms of sa...

A Study of TAS-205 for Duchenne Muscular Dystrophy

The objective of this study is to evaluate the efficacy after 24-week repeated oral doses of TAS-205 in patients with Duchenne Muscular Dystrophy (DMD) in an exploratory manner.

Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy

The purpose of this research study is to understand the walking patterns, strength and function changes of boys with Duchenne muscular dystrophy on/off corticosteroids to determine the bes...

HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne)

The safety objective of the HOPE-Duchenne trial will be to investigate the safety and tolerability of CAP-1002 administered by multi-vessel intracoronary infusion in subjects with cardiomy...

Companies [243 Associated Companies listed on BioPortfolio]

Cure Duchenne

Cure Duchenne, a national nonprofit organization located in Newport Beach, Calif., is gaining international attention for its efforts to raise funds and awareness for Duchenne â...

Jett Foundation

Based in Kingston, MA the Jett Foundation is a non-profit organization dedicated to increasing worldwide awareness of Duchenne Muscular Dystrophy with the purpose of raising and a...

Standup for the Cure

Standup for the Cure is a Non-Profit Corporation formed in 2012 which raised more than $60,000 at its inaugural May event for the Orange County Affiliate of Susan G. Komen For The...

Accelerated Cure Project

Accelerated Cure Project for Multiple Sclerosis, www.acceleratedcure.org, is a national nonprofit organization dedicated to curing Multiple Sclerosis (MS) by determining its cause...

P‐Cure Ltd.

P‐Cure develops advanced solutions that help bring proton therapy to routine clinical practice. The P-Cure system provides an integrated solution with volumetric imaging, pat...

More Information about "Cure Duchenne" on BioPortfolio

We have published hundreds of Cure Duchenne news stories on BioPortfolio along with dozens of Cure Duchenne Clinical Trials and PubMed Articles about Cure Duchenne for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Cure Duchenne Companies in our database. You can also find out about relevant Cure Duchenne Drugs and Medications on this site too.

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