Advertisement

Topics

Cure Duchenne Company Profile

21:08 EDT 20th August 2017 | BioPortfolio

Cure Duchenne, a national nonprofit organization located in Newport Beach, Calif., is gaining international attention for its efforts to raise funds and awareness for Duchenne – a devastating and lethal muscle disease in children. One in every 3,500 male births results in a child being afflicted with the disease. Nearly 20,000 boys are living with the disease in the United States alone, and many will not survive their teenage years. The disorder knows no ethnic or social boundaries.


News Articles [552 Associated News Articles listed on BioPortfolio]

Eighth Annual Champions to CureDuchenne Gala Raises More Than $378,000 Towards Finding a Cure for Duchenne Muscular Dystrophy

On April 8, hundreds gathered at The University of Texas Golf Club for a common goal, raising awareness and funds to help CureDuchenne in its mission to find a cure for Duchenne m...

New Study Published in Clinical Chemistry Evaluates Biomarker for Duchenne Muscular Dystrophy Screening in Newborn Babies

PerkinElmer, Inc. Provides Research-Use-Only Automated Immunoassay to Detect Creatine Kinase Muscle Isozyme in Dried Blood Spots A new study published in Clinical Chemistry has revealed a potential au...

STAT Plus: PTC prices its Duchenne drug at $35,000 a year, prompting new skepticism

The pricing for its Duchenne muscular dystrophy drug is well below the $89,000 that Marathon Pharmaceuticals planned to charge.

Jett Foundation Helps Provide Necessary Resources for Families Affected by Duchenne

KINGSTON, Mass., May 31, 2017 /PRNewswire-USNewswire/ -- Jett Foundation, a non-profit organization dedicated to awareness and helping fight Duchenne muscular dystrophy, recently launched the Jett Giv...

FDA Grants Orphan Drug Designation to RASRx’s Duchenne Muscular Dystrophy Drug

NEWPORT BEACH, Calif.–(BUSINESS WIRE)–RASRx announced today that the United States Food and Drug Administration (FDA) has granted an Orphan Drug Designation (ODD) for its compound RASRx190...

SB 643 Passes Senate Health Committee

The First Step to Add Duchenne Muscular Dystrophy to GHPP CureDuchenne, the leading nonprofit focused on finding a cure for Duchenne muscular dystrophy, is proud to spo...

Six-Month Results from Capricor's HOPE-Duchenne Trial to be Presented at the 2017 PPMD Annual ...

Capricor expects to launch its next clinical trial of CAP-1002 for the treatment of Duchenne muscular dystrophy in the second half of 2017, subject to Read more...

Duchenne drug poised to cost $35,000 but with major catch

For those that have not followed the story, Emflaza was successfully taken through the FDA regulatory process by Marathon as the first new treatment for Duchenne muscular dystrophy. It seemed great ne...

PubMed Articles [297 Associated PubMed Articles listed on BioPortfolio]

Development of a New Self-Reporting Instrument Measuring Benefits and Side Effects of Corticosteroids in Duchenne Muscular Dystrophy: Report from a Pilot Study.

There is no cure for Duchenne Muscular Dystrophy (DMD); treatment is symptomatic and corticosteroids slow the progression. Side effects of corticosteroids - especially the physical effects - have been...

Longitudinal Community Walking Activity in Duchenne Muscular Dystrophy.

Natural history studies for Duchenne muscular dystrophy (DMD) have not included measures of community ambulation.

New Survival Target for Duchenne Muscular Dystrophy.

We report a patient with a typical phenotype and clinical history of Duchenne muscular dystrophy who is currently 53 years old. Because of improvements in cardiopulmonary care, there has been a great ...

Spatially localized phosphorous metabolism of skeletal muscle in Duchenne muscular dystrophy patients: 24-month follow-up.

To assess the changes in phosphodiester (PDE)-levels, detected by 31P magnetic resonance spectroscopy (MRS), over 24-months to determine the potential of PDE as marker for muscle tissue changes in Duc...

Electrical impedance myography for assessment of Duchenne muscular dystrophy.

Sensitive, objective and easily applied methods for evaluating disease progression and response to therapy are needed for clinical trials in Duchenne muscular dystrophy (DMD). In this study, we evalua...

Clinical Trials [538 Associated Clinical Trials listed on BioPortfolio]

Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2

Duchenne Muscular Dystrophy (DMD) is a X-linked genetic disorder primarily affecting males, resulting in an absence of dystrophin which ultimately leads to progressive muscle degeneration....

Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy

The purpose of this study is to determine if ACE-031 is safe and well-tolerated in children with Duchenne Muscular Dystrophy (DMD) and to select the optimal doses of ACE-031 in terms of sa...

A Study of TAS-205 for Duchenne Muscular Dystrophy

The objective of this study is to evaluate the efficacy after 24-week repeated oral doses of TAS-205 in patients with Duchenne Muscular Dystrophy (DMD) in an exploratory manner.

Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy

The purpose of this research study is to understand the walking patterns, strength and function changes of boys with Duchenne muscular dystrophy on/off corticosteroids to determine the bes...

HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne)

The safety objective of the HOPE-Duchenne trial will be to investigate the safety and tolerability of CAP-1002 administered by multi-vessel intracoronary infusion in subjects with cardiomy...

Companies [250 Associated Companies listed on BioPortfolio]

Cure Duchenne

Cure Duchenne, a national nonprofit organization located in Newport Beach, Calif., is gaining international attention for its efforts to raise funds and awareness for Duchenne â...

Jett Foundation

Based in Kingston, MA the Jett Foundation is a non-profit organization dedicated to increasing worldwide awareness of Duchenne Muscular Dystrophy with the purpose of raising and a...

Standup for the Cure

Standup for the Cure is a Non-Profit Corporation formed in 2012 which raised more than $60,000 at its inaugural May event for the Orange County Affiliate of Susan G. Komen For The...

Accelerated Cure Project

Accelerated Cure Project for Multiple Sclerosis, www.acceleratedcure.org, is a national nonprofit organization dedicated to curing Multiple Sclerosis (MS) by determining its cause...

P‐Cure Ltd.

P‐Cure develops advanced solutions that help bring proton therapy to routine clinical practice. The P-Cure system provides an integrated solution with volumetric imaging, pat...

More Information about "Cure Duchenne" on BioPortfolio

We have published hundreds of Cure Duchenne news stories on BioPortfolio along with dozens of Cure Duchenne Clinical Trials and PubMed Articles about Cure Duchenne for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Cure Duchenne Companies in our database. You can also find out about relevant Cure Duchenne Drugs and Medications on this site too.

Quick Search
Advertisement
 

Relevant Topics

Rheumatology
Arthritis Fibromyalgia Gout Lupus Rheumatic Rheumatology is the medical specialty concerned with the diagnosis and management of disease involving joints, tendons, muscles, ligaments and associated structures (Oxford Medical Diction...

Pediatrics
Pediatrics is the general medicine of childhood. Because of the developmental processes (psychological and physical) of childhood, the involvement of parents, and the social management of conditions at home and at school, pediatrics is a specialty. With ...


Corporate Database Quicklinks



Searches Linking to this Company Record