'Antisense' Compound Rids Muscle Cells Of Toxic RNA: A Promising Step Toward Muscular Dystrophy Treatment
Scientists have reversed symptoms of myotonic muscular dystrophy in mice by eliminating a buildup of toxic RNA in muscle cells. The work, carried out by scientists at the University of Rochester Medical Center, Isis Pharmaceuticals Inc. and Genzyme,..
Original Article: 'Antisense' Compound Rids Muscle Cells Of Toxic RNA: A Promising Step Toward Muscular Dystrophy Treatment
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