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Companies Related to "Experimental Agent Offers First Hope Rare Genetic Disorder" [Most Relevant Company Matches] RSS

02:22 EST 27th February 2020 | BioPortfolio

Here are the most relevant search results for "Experimental Agent Offers First Hope Rare Genetic Disorder" found in our extensive corporate database of over 50,000 company records.

Showing "Experimental Agent Offers First Hope Rare Genetic Disorder" Companies 1–25 of 3,900+

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CENTOGENE

CENTOGENE unlocks the power of genetic insights to improve the quality of life of patients with rare genetic diseases. We achieve this through knowledge created by our worldwide diagnostic testing services incorporating global diversity, the world’s leading proprietary human genetic interpretation database, CentoMD® and solutions for pharmaceutical...


National Organization for Rare Disorders

Mission StatementThe National Organization for Rare Disorders (NORD), a 501(c)3 organization, is a unique federation of voluntary health organizations dedicated to helping people with rare "orphan" diseases and assisting the organizations that serve them. NORD is committed to the identification, treatment, and cure of rare disorders through programs of education, advocacy, research, and service. W...

Eating Disorder Hope


Disorder: The Rare Disease Film Festival

Global Genes

Global Genes is a non-profit organization that operates as one of the leading rare disease patient advocacy groups in the world. Global Genes promotes the needs of the Rare Disease Community under a unifying symbol of hope—the Blue Denim Genes Ribbon™. The organization was born out of humble beginnings, emerging as a grassroots movement in 2009 comprise...

DEBRA

Epidermolysis Bullosa (EB) is a rare genetic disorder characterized by the presence of extremely fragile skin and recurrent blister formation, resulting from minor mechanical friction or trauma. Secondary complications can include infections, oral ulcerations, dental decay, esophageal blistering, corneal erosions, osteoporosis and psychological trauma. Thi...

GBS/CIDP Foundation

GBS is an inflammatory disorder of the peripheral nerves and is characterized by the rapid onset of weakness and often paralysis of the legs, arms, breathing muscles and face. GBS can develop in persons of any age. CIDP is a rare disorder of the peripheral nerves with weakness occurring over two or more months and is characterized by gradually increasing weakness of the legs and, to a lesser ext...

Genetic Analysis

Genetic Analysis has developed and launched the first gene-based routine test for the mapping and diagnosis of diseases related to dysbiosis and imbalances in the bacteria in the digestive system. The company markets the GA-map™ technology to three market segments: commercial routine testing, pharma companies and the research market. Genetic Analysis ...

Zoloft

Zoloft is well tolerated and effective for the treatment of depression and certain types of anxiety disorders. Zoloft is FDA approved to treat depression, social anxiety disorder, posttraumatic stress disorder (PTSD), panic disorder, obsessive-compulsive disorder (OCD), and premenstrual dysphoric disorder (PMDD) in adults over age 18. It is also approved for OCD in children and adolescents age 6-1...

Xenon Pharmaceuticals Inc

Xenon is a privately held company located in Vancouver and has just over 70 employees. We are a leader in clinical genetic based drug discovery and development and have built a worldwide network of over 40 clinical collaborators to find and access the rare families with diseases of relevance to drug discovery. Our clinical genetic approaches are: Extreme Genetics TM: the analysis of rare families ...

Openly Rare with Paul Kidwell

Openly Rare with Paul Kidwell is a monthly podcast covering all aspects of rare diseases and will feature conversations with newsmakers and leaders from the world of biomedical and academic research, patient engagement, caregiving, rare disease patients and their families, as well as others who in some way have been touched by the growing number of rare il...

Scioderm, Inc.

Scioderm is a privately held, clinical-stage biopharmaceutical company focused on developing innovative therapies to address diseases with high need, including rare diseases. The company’s lead therapy, SD-101, is in Phase 3 development for treatment of the skin effects associated with Epidermolysis Bullosa (EB), a rare genetic connective tissue disorder. ...

AVROBIO, Inc.

AVROBIO, Inc., a leader in lentiviral-based gene therapies, is a clinical-stage company developing disruptive therapies that have the potential to transform patients’ lives with a single dose. The Company is focused on the development of its Phase 1 program in Fabry disease and pre-Phase 1/2 program in Gaucher disease, while actively building a pipeli...

Society for Experimental Biology

The Society for Experimental Biology promotes and supports all disciplines of Experimental Biology worldwide. All researchers, teachers and students who have an interest in any aspect of experimental biology are encouraged to join.SEB membership is open to scientists world-wide.The Society provides:Timely and topical meetings across the interests of the Society. A forum for experimental biologists...

Project HOPE

Founded in 1958, Project HOPE (Health Opportunities for People Everywhere) is dedicated to providing lasting solutions to health crises, with the mission of helping people to help themselves. Identifiable to many by the SS HOPE, the world’s first peacetime hospital ship, Project HOPE now conducts land-based medical training and health education progra...

Rare Disease Communications®

Rare Disease Communications® is a health care communications and media company focused on the rare disease community and dedicated to raising awareness of rare diseases and orphan drugs so that patients will be diagnosed and treated more efficiently. Rare Disease Communications® is part of the Michael J. Hennessy Associates, Inc. family of businesses, ...

Children's Rare Disease Network

The Children's Rare Disease Network (CDRN) is a non-profit advocacy group committed to connecting, educating and empowering the rare disease community, providing a link between families impacted by rare disease. The CDRN is a division of and developed by The R.A.R.E. Project which exists to promote rare disease advocacy, research and accelerated therapy development. For more information, visit w...

Onspira Therapeutics

Onspira Therapeutics is a clinical-stage biopharmaceutical company focused on the development of life-changing medicines to bring hope to patients suffering from rare pulmonary diseases. Our model leverages internal, external and shared expertise to efficiently advance promising medicines against clear and validated targets where there are unmet medical ne...

Recordati Rare Diseases Canada Inc.

Recordati Rare Diseases Canada Inc. is a biopharmaceutical company committed to providing often overlooked orphan therapies to underserved rare disease communities in Canada. Recordati Rare Diseases Canada Inc. and our sister company, Orphan Europe, are part of the rare disease business within the Recordati Group, a public global pharmaceutical company co...

Hoops of Hope

Hoops of Hope (www.hoopsofhope.org) is a 501c3 organization based in Mesa, Arizona that was founded in 2003 to raise money for AIDS orphans in Africa. Thousands of people from 17 countries have participated in Hoops of Hope events, raising more than $1.5 million to date.

Rare Disease Communications

Rare Disease Communications® is a healthcare communications and media company focused on the rare disease community and dedicated to raising awareness of rare diseases and orphan drugs so that patients will be diagnosed and treated more efficiently. Rare Disease Communications® is part of the Michael J. Hennessy Associates, Inc. family of businesses, ...

Mauli Ola Foundation

Mauli Ola Foundation (MOF) is a 501 (c) 3 nonprofit organization dedicated to providing hope and confidence to individuals living with genetic diseases. Harnessing the healing powers of the ocean, MOF introduces surfing and ocean-based activities as natural therapies. MOF is honored to hare the knowledge of the ocean, family values and community. For more ...

The Hope Heart Institute

The Hope Heart Institute was founded in 1959 by Lester R. Sauvage, MD, a world-renowned cardiovascular surgeon and research scientists. Dr. Sauvage and The Hope earned international recognition in 1962 through pioneering coronary artery bypass graft (CABG) surgery. Today, The Hope's research remains at the forefront of the cardiovascular field—and our health education publications reach nearly 5...

MoneyGram International

MoneyGram International, a leading money transfer company, enables consumers who are not fully served by traditional financial institutions to meet their financial needs. MoneyGram offers money transfer services worldwide through a global network of 334,000 agent locations – including retailers, international post offices and financial institutions â...

Pear Therapeutics

Pear Therapeutics is the leader in prescription digital therapeutics. The company’s approach is to integrate clinically-validated software applications with previously approved pharmaceuticals and treatment paradigms to provide better outcomes for patients, smarter engagement and tracking tools for clinicians, and cost-effective solutions for payers. ...


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