Topics

Companies Related to "Regenxbio Stellar Gene Therapy Innovator With Multiple Upsides" [Most Relevant Company Matches] [Advanced Search Results] RSS

10:45 EST 13th November 2019 | BioPortfolio

Here are the most relevant search results for "Regenxbio Stellar Gene Therapy Innovator With Multiple Upsides" found in our extensive corporate database of over 50,000 company records.

Showing "Regenxbio Stellar Gene Therapy Innovator With Multiple Upsides" Companies 1–25 of 2,900+

Extremely Relevant

Dimension Therapeutics, Inc.

Dimension Therapeutics, Inc. is a gene therapy company focused on developing novel treatments for patients with hemophilia and rare diseases. Dimension has built a product development pipeline based on an industry-leading adeno-associated virus (AAV) platform, and the Company is advancing multiple gene therapy programs toward clinical development. These pr...


Gene Therapy Systems (GTS)

Gene Therapy Systems, Inc. (GTS) designs, develops and commercializes gene therapy products along with other molecular biological reagents for scientists specializing in gene therapy research. GTS is the only company in the biotechnology reagent business that primarily focuses on gene therapy related products.

Dimension Therapeutics

Dimension Therapeutics is a gene therapy company focused on developing novel therapies to treat rare diseases. Launched by Fidelity Biosciences in 2013, the Dimension team comprises biotech industry veterans and renowned thought leaders in gene therapy and rare diseases. The company is focused on building its adeno-associated virus (AAV) therapeutic discov...


Relevant

Cell Genesys

Cell Genesys is a leader in the development and commercialization of innovative therapeutic products for cancer based on gene therapy technologies. The company has a broad portfolio of clinical stage product development programs, the largest patent portfolio in the gene therapy field, proprietary gene delivery technologies, and a strong balance sheet, all of which have helped position Cell Genesy...

Karolinska Institute

The primary objectives of the European Society of Gene Therapy (ESGT) are to promote basic and clinical research in gene therapy, to promote education and the exchange of information and technology related to gene transfer and therapy and to serve as a professional adviser to the community and to the regulatory bodies in Europe.

Myonexus Therapeutics

Myonexus Therapeutics is a clinical stage, rare disease gene therapy company developing first ever treatments for limb girdle muscular dystrophies (LGMDs) based on research at Nationwide Children’s Hospital, a leader in neuromuscular gene therapy discovery and translational research. Myonexus Therapeutics’ pipeline includes three clinical stage g...

Talee Bio, Inc.

Talee Bio is a development stage biopharmaceutical company focused on developing gene therapy products for the treatment of cystic fibrosis. The company is developing two inhaled gene therapy drug candidates to treat all cystic fibrosis patients: TL-101, a recombinant AAV-based gene therapy, and TL-102, a lentivirus gene therapy. The company was founded by...

Neurologix

Neurologix, Inc., a leader in the development of innovative therapies for the brain and central nervous system, utilizes gene therapy and other novel technologies. The central nervous system ("CNS") is a new and particularly exciting target for gene therapy because its unique properties prevent the successful treatment of many neurological disorders by conventional means such as drug therapy and s...

MOLOGEN AG

MOLOGEN is specializing in selected areas of Molecular Medicine. Our areas of competence are gene expression, gene therapy and bioinformatics. We are dedicated to the development of DNA expression and delivery technologies for human and veterinary applications, leading to products for gene therapy, and prophylactic and therapeutic DNA-based vaccines

RheoGene Inc

RheoGene is developing the RheoSwitch® Therapeutic System (RTS) for cell and gene therapy. RTS delivers therapeutic gene products in the patient to the right place, at the right time, and at the right dose. Despite advances in the understanding of the genetic and molecular basis of disease, there are no approved gene therapy products on the market today, in part because of the unmet need for effi...

Sangamo Therapeutics, Inc.

Sangamo Therapeutics is committed to translating ground-breaking science into genomic medicines with the potential to transform patients’ lives using gene therapy, ex vivo gene-edited cell therapy, in vivo genome editing and gene regulation. For more information about Sangamo, visit www.sangamo.com

ADVANCED CELL & GENE THERAPY, LLC

ADVANCED CELL & GENE THERAPY, LLC, is a consulting firm serving biotechnology companies, clinical laboratories, and biotechnology investors. We provide practical, experienced guidance in development, GMP/GTP manufacturing, and regulatory compliance, as well as comprehensive scientific and technical strategic analysis of business opportunities in cell, gene and tissue therapies.

IVERIC bio

IVERIC bio is a biotechnology company with a focus on the discovery and development of novel gene therapy solutions to treat orphan inherited retinal diseases with unmet medical needs. Vision is Our Mission. For more information on the Company's gene therapy and other programs, please visit www.ivericbio.com.

IVERIC bio, Inc.

IVERIC bio is a biotechnology company with a focus on the discovery and development of novel gene therapy solutions to treat orphan inherited retinal diseases with unmet medical needs. Vision is Our Mission. For more information on the Company’s gene therapy and other programs, please visit www.ivericbio.com.

Transgene

TRANSGENE is a leading integrated gene therapy company, dedicated to the discovery and development of gene delivery technologies and gene therapy products for the treatment of acquired and inherited diseases. The Company's proprietary technology platform consists of five vector families including three of viral origin - adenovirus, retrovirus, vaccinia virus - and two of non viral origin - cellula...

American Society of Gene Therapy

The American Society of Gene Therapy (ASGT) is a non-profit medical and professional organization that represents researchers and scientists devoted to the discovery of new gene therapies. ASGT was established in 1996 by Dr. George Stamatoyannopoulos, professor of medicine at the University of Washington 's School of Medicine and a group of the country's leading researchers in gene therapy. With m...

Neurogene, Inc.

Neurogene was founded to bring life-changing medicines to patients and families affected by rare neurological disorders. We partner with leading academic researchers, patient advocacy organizations and caregivers to bring therapies to patients that address the underlying genetic cause of a broad spectrum of neurological diseases where no effective treatmen...

Avigen

Avigen is a leader in the development of gene therapy products derived from adeno-associated virus ("AAV") for the treatment of inherited diseases. Avigen's proposed gene therapy products are designed for in vivo administration to achieve the production of therapeutic proteins within the body. Avigen has honed it's strategic focus on developing a broad-based proprietary gene delivery technology, A...

Neurogene Inc.

Neurogene was founded to bring life-changing medicines to patients and families affected by rare neurological disorders. We partner with leading academic researchers, patient advocacy organizations and caregivers to bring to patients therapies that address the underlying genetic cause of a broad spectrum of neurological diseases where no effective treatment options exist today. Our lead programs ...

BioMedica Inc.

Oxford BioMedica (LSE: OXB) is a biopharmaceutical company specialising in the development of novel gene-based therapeutics with a focus on the areas of oncology and neurotherapy. The Company was established in 1995 as a spin out from Oxford University, and is listed on the London Stock Exchange.Oxford BioMedica’s products use genes as the mediators of a therapeutic effect and/or immune response...

Collateral Therapeutics Incorporated

Collateral's initial non-surgical gene therapy products under investigation are designed to promote and enhance angiogenesis, a natural biological process which results in the growth of additional blood vessels, to increase levels of blood flow to oxygen-deprived tissues. The Company's angiogenic products are administered using methods of gene therapy based on non-surgical adenoviral vector delive...

INHERINET

INHERINET (Gene Therapy of Hematopoietic Stem Cells for Inherited Diseases), an initiative founded by seven European research institutions, accumulates the expertise of biomedical scientists who have a strong background in the development of all platform technologies required for successful gene therapy:State-of -the-art design and production of retroviral and lentiviral gene transfer vectors Basi...

Rocket Pharmaceuticals, Inc.

Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) (“Rocket”) is an emerging, clinical-stage biotechnology company focused on developing first-in-class gene therapy treatment options for rare, undertreated diseases. Rocket’s multi-platform development approach applies the well-established lentiviral vector (LVV) and adeno-associated viral vector (AA...

Copernicus Therapeutics Incorporated

Copernicus Therapeutics, Inc. is a privately-held company developing products for human gene therapy and vaccination. Copernicus was established in 1997 based on technologies discovered at Case Western Reserve University that provide the foundation for the use of DNA as drugs.Copernicus is not involved in gene discovery or the linkage of genetic defects to disease. Copernicus' business focuses on ...

Akouos

Akouos is a precision genetic medicine company developing gene therapies that restore and preserve hearing. Leveraging its adeno-associated viral vectors (AAV)-based gene therapy platform, Akouos is focused on developing precision therapies for forms of sensorineural hearing loss. Headquartered in Boston, the Company was founded in 2016 by world leaders in...


More From BioPortfolio on "Regenxbio Stellar Gene Therapy Innovator With Multiple Upsides"

Quick Search

Corporate Database Quicklinks