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Companies Related to "Vertex ramps spending support gene therapy manufacturing" [Most Relevant Company Matches] RSS

16:09 EST 12th December 2019 | BioPortfolio

Here are the most relevant search results for "Vertex ramps spending support gene therapy manufacturing" found in our extensive corporate database of over 50,000 company records.

Showing "Vertex ramps spending support gene therapy manufacturing" Companies 1–25 of 7,300+

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Gene Therapy Systems (GTS)

Gene Therapy Systems, Inc. (GTS) designs, develops and commercializes gene therapy products along with other molecular biological reagents for scientists specializing in gene therapy research. GTS is the only company in the biotechnology reagent business that primarily focuses on gene therapy related products.


Relevant

Vertex Pharmaceuticals Inc.

Vertex is a global biotechnology company that aims to discover, develop and commercialize innovative new medicines so people with serious diseases can lead better lives. Founded in 1989, Vertex today employs more than 2,000 people at sites around the world.  In addition to our headquarters in Massachusetts, Vertex has research and development sites and other offices in San Diego, CA; Abingd...

Talee Bio, Inc.

Talee Bio is a development stage biopharmaceutical company focused on developing gene therapy products for the treatment of cystic fibrosis. The company is developing two inhaled gene therapy drug candidates to treat all cystic fibrosis patients: TL-101, a recombinant AAV-based gene therapy, and TL-102, a lentivirus gene therapy. The company was founded by...


ADVANCED CELL & GENE THERAPY, LLC

ADVANCED CELL & GENE THERAPY, LLC, is a consulting firm serving biotechnology companies, clinical laboratories, and biotechnology investors. We provide practical, experienced guidance in development, GMP/GTP manufacturing, and regulatory compliance, as well as comprehensive scientific and technical strategic analysis of business opportunities in cell, gene and tissue therapies.

Karolinska Institute

The primary objectives of the European Society of Gene Therapy (ESGT) are to promote basic and clinical research in gene therapy, to promote education and the exchange of information and technology related to gene transfer and therapy and to serve as a professional adviser to the community and to the regulatory bodies in Europe.

Myonexus Therapeutics

Myonexus Therapeutics is a clinical stage, rare disease gene therapy company developing first ever treatments for limb girdle muscular dystrophies (LGMDs) based on research at Nationwide Children’s Hospital, a leader in neuromuscular gene therapy discovery and translational research. Myonexus Therapeutics’ pipeline includes three clinical stage g...

Blu Genes Foundation

Blu Genes Foundation was established to advance research in gene therapy for genetic disorders, offering hope where currently there is none. This need is the driving force behind Blu Genes Foundation’s mission. Gene therapy research takes dedicated time and funding support to bring treatments from bench to bedside.

Neurologix

Neurologix, Inc., a leader in the development of innovative therapies for the brain and central nervous system, utilizes gene therapy and other novel technologies. The central nervous system ("CNS") is a new and particularly exciting target for gene therapy because its unique properties prevent the successful treatment of many neurological disorders by conventional means such as drug therapy and s...

Vertex Pharmaceuticals (Europe) Limited

Vertex is a global biotechnology company that invests in scientific innovation to create transformative medicines for people with serious diseases. The company has three approved medicines that treat the underlying cause of cystic fibrosis – a rare, life-threatening genetic disease — and has several ongoing clinical and research programs in CF. Beyond CF, Vertex has a robust pipeline of...

AMT B.V

Founded in 1998 on the initiative of researchers from the Academic Medical Center (AMC) in Amsterdam, AMT has become a leader in the field of human gene therapy. A pioneer in the development of gene therapy AMT has used its scientific know-how and expertise to build up a strong research and clinical development program filling an unmet medical need for therapy of severe (orphan) diseases in the fo...

MOLOGEN AG

MOLOGEN is specializing in selected areas of Molecular Medicine. Our areas of competence are gene expression, gene therapy and bioinformatics. We are dedicated to the development of DNA expression and delivery technologies for human and veterinary applications, leading to products for gene therapy, and prophylactic and therapeutic DNA-based vaccines

ElevateBio, LLC

ElevateBio, LLC, is a Cambridge-based biotechnology company, established to create and operate a broad portfolio of cell and gene therapy companies with leading academic researchers, medical centers and entrepreneurs. ElevateBio builds single- and multi-product companies by providing scientific founders with fully-integrated bench-to-bedside capabilities i...

Dimension Therapeutics

Dimension Therapeutics is a gene therapy company focused on developing novel therapies to treat rare diseases. Launched by Fidelity Biosciences in 2013, the Dimension team comprises biotech industry veterans and renowned thought leaders in gene therapy and rare diseases. The company is focused on building its adeno-associated virus (AAV) therapeutic discov...

RheoGene Inc

RheoGene is developing the RheoSwitch® Therapeutic System (RTS) for cell and gene therapy. RTS delivers therapeutic gene products in the patient to the right place, at the right time, and at the right dose. Despite advances in the understanding of the genetic and molecular basis of disease, there are no approved gene therapy products on the market today, in part because of the unmet need for effi...

Sangamo Therapeutics, Inc.

Sangamo Therapeutics is committed to translating ground-breaking science into genomic medicines with the potential to transform patients’ lives using gene therapy, ex vivo gene-edited cell therapy, in vivo genome editing and gene regulation. For more information about Sangamo, visit www.sangamo.com

IVERIC bio

IVERIC bio is a biotechnology company with a focus on the discovery and development of novel gene therapy solutions to treat orphan inherited retinal diseases with unmet medical needs. Vision is Our Mission. For more information on the Company's gene therapy and other programs, please visit www.ivericbio.com.

IVERIC bio, Inc.

IVERIC bio is a biotechnology company with a focus on the discovery and development of novel gene therapy solutions to treat orphan inherited retinal diseases with unmet medical needs. Vision is Our Mission. For more information on the Company’s gene therapy and other programs, please visit www.ivericbio.com.

Transgene

TRANSGENE is a leading integrated gene therapy company, dedicated to the discovery and development of gene delivery technologies and gene therapy products for the treatment of acquired and inherited diseases. The Company's proprietary technology platform consists of five vector families including three of viral origin - adenovirus, retrovirus, vaccinia virus - and two of non viral origin - cellula...

The Texas Ramp Project

In 1985, the Kiwanis Club of Richardson, TX began building access ramps for residents of the Dallas area. In the years since, this effort has grown into The Texas Ramp Project, with thousands of ramps built by a network of volunteers across the state. Our volunteers say it's the most satisfying work they have ever done; liberating people imprisoned in their homes, unable to get out because of the ...

Cell Genesys

Cell Genesys is a leader in the development and commercialization of innovative therapeutic products for cancer based on gene therapy technologies. The company has a broad portfolio of clinical stage product development programs, the largest patent portfolio in the gene therapy field, proprietary gene delivery technologies, and a strong balance sheet, all of which have helped position Cell Genesy...

American Society of Gene Therapy

The American Society of Gene Therapy (ASGT) is a non-profit medical and professional organization that represents researchers and scientists devoted to the discovery of new gene therapies. ASGT was established in 1996 by Dr. George Stamatoyannopoulos, professor of medicine at the University of Washington 's School of Medicine and a group of the country's leading researchers in gene therapy. With m...

Neurogene, Inc.

Neurogene was founded to bring life-changing medicines to patients and families affected by rare neurological disorders. We partner with leading academic researchers, patient advocacy organizations and caregivers to bring therapies to patients that address the underlying genetic cause of a broad spectrum of neurological diseases where no effective treatmen...

Avigen

Avigen is a leader in the development of gene therapy products derived from adeno-associated virus ("AAV") for the treatment of inherited diseases. Avigen's proposed gene therapy products are designed for in vivo administration to achieve the production of therapeutic proteins within the body. Avigen has honed it's strategic focus on developing a broad-based proprietary gene delivery technology, A...

Neurogene Inc.

Neurogene was founded to bring life-changing medicines to patients and families affected by rare neurological disorders. We partner with leading academic researchers, patient advocacy organizations and caregivers to bring to patients therapies that address the underlying genetic cause of a broad spectrum of neurological diseases where no effective treatment options exist today. Our lead programs ...

Collateral Therapeutics Incorporated

Collateral's initial non-surgical gene therapy products under investigation are designed to promote and enhance angiogenesis, a natural biological process which results in the growth of additional blood vessels, to increase levels of blood flow to oxygen-deprived tissues. The Company's angiogenic products are administered using methods of gene therapy based on non-surgical adenoviral vector delive...


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