Orphan Europe (UK) Ltd. Company Profile

21:40 EDT 19th June 2018 | BioPortfolio

Orphan Europe was started with the objective of providing orphan drugs to patients afflicted by rare disorders.Over the years an information network has been established to increase the awareness about rare disorders among healthcare professionals. The company has committed itself to provide support necessary to those working in this field. This is achieved through an extensive collaboration with experts in respective disease areas. Information and educational services can be provided upon request.
In another approach to strengthen the Orphan Drug status in Europe the company has provided input to the recently enacted European Orphan Drug Legislation.
We have highly experienced staff in our medical, regulatory and marketing departments with previous experience from major pharma companies. Being a small company allows us to be flexible and act rapidly. We are taking advantage of this rapid effective approach in our objective of providing healthcare professionals, and ultimately patients, with treatments for rare disorders.


Isis House 43 Station Road
United Kingdom


Phone: 44 (0) 1491 414 333
Fax: 44 (0) 1491 414 443

News Articles [379 Associated News Articles listed on BioPortfolio]

Research shows differences in orphan drug availability in Europe

A study suggests that the availability of orphan drugs varies significantly between different countries in Europe. Conducted by the University...Read More... The post Research shows differences in orp...

Disparity in availability of orphan meds in Europe

The availability of orphan medicines varies significantly between different European countries, a new…

Is an orphan medicine still an orphan once it gets on the market?

The European Medicines Agency (EMA) will be publishing, as of today, a so-called orphan maintenance assessment…

News and press releases: Is an orphan medicine still an orphan once it gets on the market?

EMA publishes additional reports on decision-making for orphan medicines; initiative addresses requests from stakeholders

Orphan drug status for new compound 'great news' says Amryt Pharma PLC's COO

Amryt Pharma PLC (LON:AMYT) has been granted orphan drug status in the US for  a compound called AP102 to treat patients with the excess growth condition acromegaly. Chief operating officer Ror...

Cytheris: Encouraging responses and orphan drug designation in Europe for CYT107 for the treatment of PML

In this episode of PharmaTelevision News Review, filmed at #BIO2012 Convention in Boston, Fintan Walton talks to Damian Marron, CEO of Cytheris about encouraging responses and orphan drug designatio...

Astellas’ gilteritinib gets orphan designation in Europe for acute myeloid leukaemia

Astellas Pharma's gilteritinib has secured orphan designation from the European Commission (EC) to treat patients with acute myeloid leukaemia (AML).

Orphan medicine policies in 24 European countries

Drugs known as “orphan” drugs are those used to treat rare disease.  However, how “rare” is rare disease?  In Europe, a rare disease is one affecting 5 or fewer people per 10...

Drugs and Medications [8 Associated Drugs and Medications listed on BioPortfolio]

Nasal decongestant [SUPERVALU INC.]

Equaline 44-112

Carbaglu [Orphan Europe, SARL]

These highlights do not include all the information needed to use CARBAGLU safely and effectively.  See full prescribing information for CARBAGLU.   CARBAGLU (carglumic acid) TabletsInitial U.S. App...

Nizatidine [Dispensing Solutions Inc.]

Nizatidine Capsules USP Rx only


Akne-mycin (Erythromycin)

Kepivance [Swedish Orphan Biovitrum AB (publ)]

These highlights do not include all the information needed to use Kepivance safely and effectively. See full prescribing information for Kepivance.Kepivance® (palifermin) For injection, for intraveno...

PubMed Articles [399 Associated PubMed Articles listed on BioPortfolio]

Orphan drugs: trends and issues in drug development.

Research in rare diseases has contributed substantially toward the current understanding in the pathophysiology of the common diseases. However, medical needs of patients with rare diseases have alway...

The genomic history of southeastern Europe.

Farming was first introduced to Europe in the mid-seventh millennium bc, and was associated with migrants from Anatolia who settled in the southeast before spreading throughout Europe. Here, to unders...

Orphan G protein-coupled receptors: The role in CNS disorders.

There are various types of receptors in the central nervous system (CNS). G protein-coupled receptors (GPCRs) have the highest expression with a wide range of physiological functions. A newer sub grou...

Psychological wellbeing of children at public primary schools in Jimma town: An orphan and non-orphan comparative study.

Orphans face multiple challenges including insufficient food, shelter, schooling, and medical care. Most research on orphans in developing countries concentrates on nutrition and health status. The pr...

Infectious disease profiles of Syrian and Eritrean migrants presenting in Europe: A systematic review.

In the past decade, a large influx of migrants presented in Europe. Their country of origin was mainly either Syria or Eritrea. Public health institutions in host countries in Europe are challenged to...

Clinical Trials [607 Associated Clinical Trials listed on BioPortfolio]

Safety and Feasibility of Normothermic Machine Perfusion to Rescue Orphan Livers

Orphan livers are organs that have been declined for clinical use by all centers due to their marginality. The current standard of care of liver preservation before transplant is cold stor...

Orphan Europe Carbaglu® Surveillance Protocol

The purpose of this study is to conduct post-marketing surveillance of carglumic acid (Carbaglu) to obtain long-term clinical safety information. Carglumic acid was approved by the United ...

Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A

This is an open, Phase I / II clinical trial to evaluate the safety and efficacy of a hematopoietic gene therapy procedure with an orphan drug consisting of a lentiviral vector carrying th...

In-market Utilisation of Liraglutide Used for Weight Management in Europe: a Retrospective Medical Record Review Study

This study is conducted in Europe. The aim of this study is to investigate usage of liraglutide for weight management in clinical practice.

RITE-EUROPE (Radiofrequency-Induced Thermochemotherapy Effect-EUROPE)

This multicenter, prospective, single-arm, phase 3 study will assess the proportion of disease-free patients, starting from administration of the first study treatment to at least 12-month...

Companies [946 Associated Companies listed on BioPortfolio]

AOP Orphan Pharmaceuticals AG

AOP Orphan is a multinational company with headquarters in Vienna, Austria, focusing on clinical research, development and distribution of medicines for rare and complex diseases....

Orphan Europe (UK) Ltd.

Orphan Europe was started with the objective of providing orphan drugs to patients afflicted by rare disorders.Over the years an information network has been established to increase the awareness abou...

Orphan Medical Incorporated

Orphan Medical Incorporated is a development stage company, was formed to acquire, develop and market products of high medical value intended to address inadequately treated or uncommon diseases of we...

Santhera Pharmaceuticals Holding Ltd

Santhera Pharmaceuticals is a Swiss biopharmaceutical company focusing on the discovery, development and marketing of small molecule pharmaceutical products for the treatment of neuromuscular diseases...

Orphan Technologies

Orphan Technologies is dedicated to developing novel therapies to dramatically improve the lives of patients suffering from the rare disorder, homocystinuria and related diseases....

More Information about "Orphan Europe (UK) Ltd." on BioPortfolio

We have published hundreds of Orphan Europe (UK) Ltd. news stories on BioPortfolio along with dozens of Orphan Europe (UK) Ltd. Clinical Trials and PubMed Articles about Orphan Europe (UK) Ltd. for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Orphan Europe (UK) Ltd. Companies in our database. You can also find out about relevant Orphan Europe (UK) Ltd. Drugs and Medications on this site too.

Quick Search


Relevant Topics

Health care (or healthcare) is the diagnosis, treatment, and prevention of disease, illness, injury, and other physical and mental impairments in humans. Health care is delivered by practitioners in medicine, chiropractic, dentistry, nursing, pharmacy, a...

Collaborations in biotechnology
Commercial and academic collaborations are used throughout the biotechnology and pharmaceutical sector to enhance research and product development. Collaborations can take the form of research and evaluation agreements, licensing, partnerships etc. ...

Pharmacy is the science and technique of preparing as well as dispensing drugs and medicines. It is a health profession that links health sciences with chemical sciences and aims to ensure the safe and effective use of pharmaceutical drugs. The scope of...

Corporate Database Quicklinks

Searches Linking to this Company Record