Information Centre for Rare Diseases and Orphan Drugs Company Profile

18:38 EST 14th December 2018 | BioPortfolio

Information Centre for Rare Diseases and Orphan Drugs (ICRDOD) is a free educational and information service in Bulgarian and English languages, providing personalized replies to requests from patients, families and medical professionals.
Any medical or health information, provided and hosted on this site is given by medically trained and qualified professionals. The information provided on this site is designed to support, not replace, the relationship that exists between a patient/site visitor and his/her doctor. Confidentiality of data relating to individual patients and visitors to ICRDOD, including their identity, is respected by this website. We undertake to honour or exceed the legal requirements of medical/health information privacy that apply in Bulgaria.

ICRDOD is a project and activity of the Bulgarian Association for Promotion of Education and Science (BAPES) - a non-government non-profit organization, registered under the Bulgarian law on legal persons with non-profit purposes in 2003. For the realization of this website, BAPES utilizes its own funding, received from private donors. The director and all consultants of ICRDOD are contributing on volunteer basis.


4 Bratia Svestarovi str.


Phone: 359-897-858870

News Articles [4040 Associated News Articles listed on BioPortfolio]

Orphan Drugs and Rare Diseases Conference 2018

17 - 18 October, London, UK. Patients with rare diseases cannot continue to be overlooked because of costly therapies and have the same rights to treatment as any other patient. At this year's Orphan ...

[Viewpoint] Outrageous prices of orphan drugs: a call for collaboration

Few instances of a single act of legislation have shifted industrial policy in the pharmaceutical industry like the Orphan Drugs Act did when it was signed in the USA in 1983. The Act was written to f...

Balancing expectations: An unmet need in the orphan disease arena

There are between 6000 and 8000 rare diseases in the world, and one in ten people in Europe and the US have a rare disease; 75% of rare diseases affect children, and 30% of rare disease patients die b...

FDA Awards 12 Grants for Drug Development for Rare Diseases

NewsThe FDA awarded the grants through the Orphan Products Clinical Trials Grants Program.Contributed Author: 

NORD Rare Diseases and Orphan Products Breakthrough Summit

October 15-16, 2018 in Washington, D.C. During the 2018 NORD Rare Summit, over 700 leaders from FDA, NIH, industry, patient groups, payers and research institutions will address the New Era of Patient...

Prescribe Robust Distribution to Commercialize Your Orphan Drug

Finding a home for your biopharmaceutical company’s new orphan drug doesn’t just happen after it is FDA approved. The successful commercialization of your promising new drug requires a focused and...

Government Investigation Finds Flaws in the FDA's Orphan Drug Program

The investigation examines the booming orphan drug business and how drug makers have rushed into the marketplace with hundreds of drugs for rare diseases. Kaiser Health News

How a Collaborative Ecosystem is Driving the Development of Successful Therapies in Rare Disease Research

ArticleResearch models are an essential component to understanding the biology of specific rare diseases.Contributed A

PubMed Articles [5636 Associated PubMed Articles listed on BioPortfolio]

Disease and economic burden for rare diseases in Taiwan: A longitudinal study using Taiwan's National Health Insurance Research Database.

High-cost orphan drugs are becoming increasingly available to treat rare diseases that affect a relatively small population. Little attention has been given to the prevalence of rare diseases and thei...

Innovative therapeutic approaches for hereditary neuromuscular diseases.

Advances in the understanding of the genetic mechanisms and pathophysiology of neuromuscular diseases have recently led to the development of new, innovative and often mutation-specific therapeutic ap...

Dose-Finding Studies Among Orphan Drugs Approved in the EU: A Retrospective Analysis.

In the development process for new drugs, dose-finding studies are of major importance. Absence of these studies may lead to failed phase 3 trials and delayed marketing authorization. In our study we ...

Insights into the Pharmaceuticals and Mechanisms of Neurological Orphan Diseases: Current Status and Future Expectations.

Several rare or orphan diseases have been characterized that singly affect low numbers of people, but cumulatively reach ∼6% - 10% of the population in Europe and in the United States. Human genetic...

Treatment networks and associations of patients with rare diseases.

Patients' associations are an example of biosocial groups, since their formation is motivated by common biological characteristics, such as rare diseases, and they are sometimes included in social mov...

Clinical Trials [8277 Associated Clinical Trials listed on BioPortfolio]

Diagnostic Research in Patients With Rare Diseases - Solving the Unsolved Rare Diseases

The DiRiP study will enroll patients (n = 3500) with unclear rare diseases and suspected genetic reasons. In group 1 (n = 500) subjects are clinically characterized in the context of outpa...

Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in Children

The incidence of rare diseases is extremely low, the disease is numerous, the symptoms are serious, and the detection technology is complicated. Countries have different definitions of rar...

Development of In Vitro Functional Assays From Primary Cells of Patients With Monogenic Diseases

The objective of this project is to build a collection of biological samples consisting of fibroblasts and primary keratinocytes from patients with orphan monogenic diseases and to use the...

Finding Genes for Rare Diseases

This study will help the investigator understand the pathogenesis of different rare genetic conditions and to establish database of rare genetic databases. This would ultimately help to pr...

Gene Discovery Core, The Manton Center

The Gene Discovery Core at The Manton Center for Orphan Disease Research based at Boston Children's Hospital studies families with rare, poorly understood or undiagnosed, but suspected gen...

Companies [2995 Associated Companies listed on BioPortfolio]

Information Centre for Rare Diseases and Orphan Drugs

Information Centre for Rare Diseases and Orphan Drugs (ICRDOD) is a free educational and information service in Bulgarian and English languages, providing personalized replies to requests from patient...

Recordati Rare Diseases Canada Inc.

Recordati Rare Diseases Canada Inc. is a biopharmaceutical company committed to providing often overlooked orphan therapies to underserved rare disease communities in Canada. Reco...

AOP Orphan Pharmaceuticals AG

AOP Orphan is a multinational company with headquarters in Vienna, Austria, focusing on clinical research, development and distribution of medicines for rare and complex diseases....

National Organization for Rare Disorders

Mission StatementThe National Organization for Rare Disorders (NORD), a 501(c)3 organization, is a unique federation of voluntary health organizations dedicated to helping people with rare "orphan" di...

Rare Disease Communications

Rare Disease Communications® is a healthcare communications and media company focused on the rare disease community and dedicated to raising awareness of rare diseases and orph...

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