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Cure Duchenne Company Profile

10:30 EDT 20th October 2017 | BioPortfolio

Cure Duchenne, a national nonprofit organization located in Newport Beach, Calif., is gaining international attention for its efforts to raise funds and awareness for Duchenne – a devastating and lethal muscle disease in children. One in every 3,500 male births results in a child being afflicted with the disease. Nearly 20,000 boys are living with the disease in the United States alone, and many will not survive their teenage years. The disorder knows no ethnic or social boundaries.


News Articles [427 Associated News Articles listed on BioPortfolio]

Sarepta Therapeutics: Backing A Cure For Duchenne Muscular Dystrophy

CureDuchenne Release: 7th Annual Getzlaf Golf Shootout Raises More Than $546,000 To Help Find A Cure For Duchenne Muscular Dystrophy

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Parent Project Muscular Dystrophy Announces Duchenne Action Month this September

HACKENSACK, N.J., Sept. 1, 2017 /PRNewswire-USNewswire/ -- Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne), will...

Study: Drug Candidate Demonstrates Efficacy in Duchenne Muscular Dystrophy

NewsBiophytis clinical stage drug-candidate sarconeos demonstrates efficacy in preclinical models of Duchenne muscular dystrophy. Duchenne muscular dystrophy is a new 'Orphan' indication for Sarconeos...

FDA Grants Orphan Drug Designation to RASRx’s Duchenne Muscular Dystrophy Drug

NEWPORT BEACH, Calif.–(BUSINESS WIRE)–RASRx announced today that the United States Food and Drug Administration (FDA) has granted an Orphan Drug Designation (ODD) for its compound RASRx190...

Duchenne Muscular Dystrophy: The Race For The $1bn Opportunity

With three products now approved in Europe and/or the US for Duchenne Muscular Dystrophy, an FDA decision pending on PCT...   

US drug maker sues to force Ireland to offer expensive Duchenne’s treatment

The American pharmaceutical firm PTC Therapeutics is suing Ireland’s Health Service Executive (HSE) over its decision not to fund drugs for two boys with Duchenne muscular dystrophy (DMD).PTC’s dr...

7th Annual Getzlaf Golf Shootout Raises More than $546,000 To Help Find a Cure for Duchenne Muscular Dystrophy

-- Anaheim Ducks Captain Ryan Getzlaf and Wife Paige Getzlaf Continue their Support of CureDuchenne -- The 7th Annual Getzlaf Golf Shootout benefiting CureDuchenne ...

PubMed Articles [278 Associated PubMed Articles listed on BioPortfolio]

Development of a New Self-Reporting Instrument Measuring Benefits and Side Effects of Corticosteroids in Duchenne Muscular Dystrophy: Report from a Pilot Study.

There is no cure for Duchenne Muscular Dystrophy (DMD); treatment is symptomatic and corticosteroids slow the progression. Side effects of corticosteroids - especially the physical effects - have been...

Longitudinal Community Walking Activity in Duchenne Muscular Dystrophy.

Natural history studies for Duchenne muscular dystrophy (DMD) have not included measures of community ambulation.

Spatially localized phosphorous metabolism of skeletal muscle in Duchenne muscular dystrophy patients: 24-month follow-up.

To assess the changes in phosphodiester (PDE)-levels, detected by 31P magnetic resonance spectroscopy (MRS), over 24-months to determine the potential of PDE as marker for muscle tissue changes in Duc...

Energy expenditure, body composition, and prevalence of metabolic disorders in patients with Duchenne muscular dystrophy.

Duchenne muscular dystrophy (DMD) is a severe muscular disease characterized by progressive loss of functional muscle mass followed by changes in body composition.

Parents' Reactions to the Diagnosis of Duchenne Muscular Dystrophy: Associations Between Resolution, Family Functioning, and Child Behavior Problems.

Duchenne muscular dystrophy (DMD) is the most frequent inherited form of muscular dystrophy during childhood. DMD is a severe and progressive disease. Children initially have no symptoms, but the diag...

Clinical Trials [549 Associated Clinical Trials listed on BioPortfolio]

Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2

Duchenne Muscular Dystrophy (DMD) is a X-linked genetic disorder primarily affecting males, resulting in an absence of dystrophin which ultimately leads to progressive muscle degeneration....

Study of ACE-031 in Subjects With Duchenne Muscular Dystrophy

The purpose of this study is to determine if ACE-031 is safe and well-tolerated in children with Duchenne Muscular Dystrophy (DMD) and to select the optimal doses of ACE-031 in terms of sa...

A Study of TAS-205 for Duchenne Muscular Dystrophy

The objective of this study is to evaluate the efficacy after 24-week repeated oral doses of TAS-205 in patients with Duchenne Muscular Dystrophy (DMD) in an exploratory manner.

Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy

The purpose of this research study is to understand the walking patterns, strength and function changes of boys with Duchenne muscular dystrophy on/off corticosteroids to determine the bes...

HOPE-Duchenne (Halt cardiomyOPathy progrEssion in Duchenne)

The safety objective of the HOPE-Duchenne trial will be to investigate the safety and tolerability of CAP-1002 administered by multi-vessel intracoronary infusion in subjects with cardiomy...

Companies [253 Associated Companies listed on BioPortfolio]

Cure Duchenne

Cure Duchenne, a national nonprofit organization located in Newport Beach, Calif., is gaining international attention for its efforts to raise funds and awareness for Duchenne â...

Jett Foundation

Based in Kingston, MA the Jett Foundation is a non-profit organization dedicated to increasing worldwide awareness of Duchenne Muscular Dystrophy with the purpose of raising and a...

Standup for the Cure

Standup for the Cure is a Non-Profit Corporation formed in 2012 which raised more than $60,000 at its inaugural May event for the Orange County Affiliate of Susan G. Komen For The...

Accelerated Cure Project

Accelerated Cure Project for Multiple Sclerosis, www.acceleratedcure.org, is a national nonprofit organization dedicated to curing Multiple Sclerosis (MS) by determining its cause...

P‐Cure Ltd.

P‐Cure develops advanced solutions that help bring proton therapy to routine clinical practice. The P-Cure system provides an integrated solution with volumetric imaging, pat...

More Information about "Cure Duchenne" on BioPortfolio

We have published hundreds of Cure Duchenne news stories on BioPortfolio along with dozens of Cure Duchenne Clinical Trials and PubMed Articles about Cure Duchenne for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Cure Duchenne Companies in our database. You can also find out about relevant Cure Duchenne Drugs and Medications on this site too.

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