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Rare Disease Communications® Company Profile

04:12 EST 23rd January 2020 | BioPortfolio

Rare Disease Communications® is a health care communications and media company focused on the rare disease community and dedicated to raising awareness of rare diseases and orphan drugs so that patients will be diagnosed and treated more efficiently. Rare Disease Communications® is part of the Michael J. Hennessy Associates, Inc. family of businesses, based in Cranbury, N.J. MJH Associates is dedicated to improving quality of life through healthcare education, research and communication. To learn more about MJH Associates, visit http://www.mjhassoc.com and for Rare Disease Communications, visit: www.raredr.com


News Articles [1598 Associated News Articles listed on BioPortfolio]

Developing Orphan Products: FDA and Rare Disease Day

February 28, 2009 is World Rare Disease Day, an important time for bringing attention to the needs of people with rare diseases

BioMarin's Very-Rare Disease Treatment Approved in China

BioMarin, a San Francisco area rare disease biopharma, reported China's NMPA approved Vimizim® (elosulfase alfa) to treat patients with mucopolysaccharidosis type IVA (MPS IVA), a rare disease als...

New Database Shows 'Rare' Diseases Are Not So Rare Worldwide

TUESDAY, Oct. 29, 2019 -- More than 300 million people worldwide -- or 4% of the population -- have a rare disease, a new study finds. A disease is considered rare when it affects fewer than five in 1...

FDA Speeds Innovation in Rare Disease Therapies

The Food and Drug Administration Office of Orphan Products Development is launching web-based educational resources for patients and industry on rare disease topics. The page debuts on International R...

Pelosi’s radical plan would leave patients with rare pediatric diseases behind

There are about 7,000 rare diseases and half of these affect children. According to the National Institutes of Health (NIH), 30 million Americans, or 10 percent of the population, have one...

Cambridge Rare Disease Summit 2017

Our friends at the Cambridge Rare Disease Network are holding their 3rd annual International Rare Disease Summit. The Network was co-founded by one of our Leaders of Tomorrow, Dr Tim Guilliams.

Alexion's Soliris adds new approval in rare disease NMOSD

First ever drug approved for rare autoimmune disease

Possible new treatment strategy against progeria

(Karolinska Institutet) Progeria is a very rare disease that affects about one in 18 million children and results in premature aging and death in adolescence from complications of cardiovascular disea...

Drugs and Medications [1 Associated Drugs and Medications listed on BioPortfolio]

Sterile water [genentech, inc.]

Sterile Water for Injection, USP

PubMed Articles [3760 Associated PubMed Articles listed on BioPortfolio]

Objectivity in rare disease research: A philosophical approach.

Individuals living with rare conditions are faced with important challenges derived from the rarity of their conditions and aggravated by the low priority given to rare disease research. However, curr...

Statistical considerations for rare diseases drug development.

One of the most challenges for rare disease clinical trials is probably the availability of a small patient population. It is then a great concern on how to conduct clinical trials with a small number...

Health systems sustainability in the framework of rare diseases actions. Actions on educational programmes and training for professionals and patients.

Rare disease community is one of the largest patient populations in the world estimated to be 350 million of people. Collectively common, rare diseases pose a significant medical and economic burden f...

A UK reported case of Graves' disease with thyroid hemiagenesis.

We present a rare case of a 31-year-old patient with Graves' disease with agenesis of the left thyroid lobe. The patient was managed with a right hemithyroidectomy and isthmusectomy as definitively tr...

Recurrent anti-GBM disease with T-cell large granular lymphocytic leukemia: A case report.

Anti-glomerular basement membrane disease (anti-GBM disease) is a rare small vessel vasculitis caused by autoantibodies directed against the glomerular and alveolar basement membranes. Anti-GBM diseas...

Clinical Trials [4515 Associated Clinical Trials listed on BioPortfolio]

Multi-center Clinical Study on the Diagnosis and Treatment Management of Rare Neurological Disease in Children

The incidence of rare diseases is extremely low, the disease is numerous, the symptoms are serious, and the detection technology is complicated. Countries have different definitions of rar...

Registration Study for Rare Type of Pulmonary Hypertension

Our knowledge on the rare type of pulmonary hypertension which can not be explained by left heart disease, respiratory disease or congenital heart disease is very limited. Investigators ai...

Functional Genomics of Rare Genetic Diseases: Realization of Innovative Tools With High Diagnostic Power

The project aims to improve the understanding of a significant group of rare diseases both from a genetic/diagnostic and clinical/experimental point of view and aims to develop one or more...

Multi-level Communications and Access Strategies to Improve the Food Environment

The overarching goal of B'More Healthy Retail Rewards (BHRR) is to develop, implement, and evaluate a pilot multi-level communications and pricing intervention to improve access to and con...

French National Registry of Rare Peritoneal Surface Malignancies

Despite advances in the management of and changes in clinical practice, little is known about the epidemiology, patterns of care and outcomes of rare peritoneal surface malignancies patien...

Companies [1720 Associated Companies listed on BioPortfolio]

Rare Disease Communications®

Rare Disease Communications® is a health care communications and media company focused on the rare disease community and dedicated to raising awareness of rare diseases and orp...

Rare Disease Communications

Rare Disease Communications® is a healthcare communications and media company focused on the rare disease community and dedicated to raising awareness of rare diseases and orph...

Children's Rare Disease Network

The Children's Rare Disease Network (CDRN) is a non-profit advocacy group committed to connecting, educating and empowering the rare disease community, providing a link between families impacted by ra...

Openly Rare with Paul Kidwell

Openly Rare with Paul Kidwell is a monthly podcast covering all aspects of rare diseases and will feature conversations with newsmakers and leaders from the world of biomedical an...

Recordati Rare Diseases Canada Inc.

Recordati Rare Diseases Canada Inc. is a biopharmaceutical company committed to providing often overlooked orphan therapies to underserved rare disease communities in Canada. Reco...

More Information about "Rare Disease Communications®" on BioPortfolio

We have published hundreds of Rare Disease Communications® news stories on BioPortfolio along with dozens of Rare Disease Communications® Clinical Trials and PubMed Articles about Rare Disease Communications® for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Rare Disease Communications® Companies in our database. You can also find out about relevant Rare Disease Communications® Drugs and Medications on this site too.

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Health care (or healthcare) is the diagnosis, treatment, and prevention of disease, illness, injury, and other physical and mental impairments in humans. Health care is delivered by practitioners in medicine, chiropractic, dentistry, nursing, pharmacy, a...


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