Advertisement

Topics

Rocket Pharmaceuticals, Inc. Company Profile

08:43 EDT 22nd April 2018 | BioPortfolio

Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) (“Rocket”) is an emerging, clinical-stage biotechnology company focused on developing first-in-class gene therapy treatment options for rare, undertreated diseases. Rocket’s multi-platform development approach applies the well-established lentiviral vector (LVV) and adeno-associated viral vector (AAV) gene therapy platforms. Rocket's lead clinical program is a LVV-based gene therapy for the treatment of Fanconi Anemia (FA), a difficult to treat genetic disease that leads to bone marrow failure and potentially cancer. Preclinical studies of additional bone marrow-derived disorders are ongoing and target Pyruvate Kinase Deficiency (PKD), Leukocyte Adhesion Deficiency-I (LAD-I) and Infantile Malignant Osteopetrosis (IMO). Rocket is also developing an AAV-based gene therapy program for an undisclosed rare pediatric disease.


News Articles [580 Associated News Articles listed on BioPortfolio]

The Alt Rocket Tech That May One Day Take Humans to Mars

On Feb. 6, SpaceX made history when it launched its Falcon Heavy rocket from Cape Canaveral in Florida. It now reigns as the biggest and most powerful rocket in the world. Elon Musk, the messianic CEO...

Rocket Pharmaceuticals Announces Participation in a Fireside Chat at the Leerink Partners 7th Annual Global Healthcare Conference

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) (“Rocket”), a leading U.S.-based multi-platform gene therapy company, today announced that Gaurav Shah, M.D., Chief Executiv...

Rocket Pharmaceuticals to Present at the Cowen & Company 38th Annual Health Care Conference

Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) (“Rocket”), a leading U.S.-based multi-platform gene therapy company, today announced that Gaurav Shah, M.D., Chief Executive...

Rocket Pharmaceuticals Announces Participation in Fireside Chat at Evercore ISI Biopharma Catalyst/Deep Dive Conference

Rocket Pharmaceuticals, Ltd. (Rocket), a leading U.S.-based multi-platform gene therapy company, today announced that Gaurav Shah, M.D., Chief Executive Officer of Rocket, ...

Photos: SpaceX successfully launches new Falcon Heavy rocket carrying Tesla Roadster

The world’s newest and most powerful rocket had its maiden launch on Tuesday afternoon as SpaceX launched the Falcon Heavy rocket for the first time.

Gaza rocket hits Israeli town: army

A rocket fired from the Palestinian Gaza Strip enclave hit the southern Israel town of Sderot on Friday night, the Israeli army said, but refused to comment on possible casualties. Israel's national ...

Rocket Pharmaceuticals posts $19.6 million annual net loss

Rocket Pharmaceuticals, which recently merged with Inotek Pharmaceuticals, reported a net loss of $19.6 million, or $219.49 per share, in 2017 compared with a net loss of $7.6 million, or $84.43 per s...

Man Plans To Launch Himself In Homemade Rocket Funded By Flat-Earthers

A self-taught rocket engineer who claims he believes the earth is flat plans to launch himself nearly 2,000 feet in the air on a homemade steam rocket this Saturday.

Drugs and Medications [272 Associated Drugs and Medications listed on BioPortfolio]

Iontophoresis [ROCKET ELECTRIC CO., LTD.]

Drug Facts

Xarelto [Janssen Pharmaceuticals, Inc.]

These highlights do not include all the information needed to use XARELTO (rivaroxaban) safely and effectively. See full prescribing information for XARELTO. XARELTO (rivaroxaban) tablets, for oral u...

Pur-wash [Niagara Pharmaceuticals Inc.]

Pur-Wash

Bacitracin [Qualitest Pharmaceuticals]

Bacitracin Ointment, USP

Pur-wash [Niagara Pharmaceuticals Inc.]

Pur-Wash Purified Water, 98.3% Ophthalmic Solution Eyewash

PubMed Articles [132 Associated PubMed Articles listed on BioPortfolio]

Suspended solids moderate the degradation and sorption of waste water-derived pharmaceuticals in estuarine waters.

This study focuses on the fate of pharmaceuticals discharged into an estuarine environment, particularly into the Turbidity Maximum Zone (TMZ). Batch experiments were set up to investigate the factors...

Genetics of familial hypercholesterolemia: a tool for development of novel lipid lowering pharmaceuticals?

Familial hypercholesterolemia is characterized by high LDL cholesterol and an elevated risk to develop coronary heart disease. Mutations in LDL receptor-mediated cholesterol uptake are the main cause ...

Post-production handling and administration of protein pharmaceuticals and potential instability issues.

The safety and efficacy of protein pharmaceuticals depend not only on biological activity, but also on purity levels. Impurities may be process related due to limitations in manufacturing, or product ...

A General Strategy for Site-Selective Incorporation of Deuterium and Tritium into Pyridines, Diazines and Pharmaceuticals.

Methods to incorporate deuterium and tritium atoms into organic molecules are valuable for medicinal chemistry. The prevalence of pyridines and diazines in pharmaceuticals means that new ways to label...

Environmental concentrations of pharmaceuticals directly affect phytoplankton and effects propagate through trophic interactions.

Pharmaceuticals are found in freshwater ecosystems where even low concentrations in the range of ng Lmay affect aquatic organisms. In the current study, we investigated the effects of chronic exposure...

Clinical Trials [218 Associated Clinical Trials listed on BioPortfolio]

Rocket® Pleural Catheters: QOL, Feasibility and Satisfaction in Recurrent MPE Patients

This study will take place in Ottawa, Ontario, and will include 100 patients who are receiving tunnelled pleural catheters to treat their symptoms of MPE. The aim of this study is to evalu...

Study Comparing Citalopram Hydrobromide Tablets 40 mg (Torrent Pharmaceuticals Ltd) and RLD Tablets 40 mg (Manufactured By Forest Pharmaceuticals Inc, Missouri) in 24+2 Normal Healthy Male Subjects in Fed Condition

- Objective: - The objective of this study is to compare the rate and extent of absorption of the Test Product, Citalopram Hydrobromide 40 mg (Torrent Pharmaceutical Li...

Bioequivalence Study of Torrent Pharmaceuticals Ltd.'s Rosuvastatin Calcium Tablets Under Fed Conditions

Subjects to compare the single dose bioavailability of Torrent's Rosuvastatin Calcium Tablets 40 mg and Crestor® 40 mg Tablets of AstraZeneca Pharmaceuticals LP, USA. Dosing periods of st...

Cilostazol 50 mg Tablets Under Fasting Conditions

This study will compare the relative bioavailability (rate and extent of absorption) of 50 mg Cilostazol Tablets manufactured by TEVA Pharmaceuticals Industries Ltd. and distributed by TEV...

Study Comparing Citalopram Hydrobromide Tablets 40 mg (Torrent Pharmaceuticals Ltd) and RLD Tablets 40 mg (Manufactured By Forest Pharmaceuticals Inc, Missouri) in 24+2 Normal Healthy Male Subjects Under Fasting Condition

- Objective: - To compare the rate and extent of absorption of Citalopram Hydrobromide Tablets 40 mg: Test Product: Citalopram Hydrobromide Tablets 40 mg manufactured b...

Companies [1313 Associated Companies listed on BioPortfolio]

Rocket Pharmaceuticals, Ltd.

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) (“Rocket”) is an emerging, clinical-stage biotechnology company focused on developing first-in-class gene therapy treatment o...

Rocket Pharmaceuticals, Inc.

Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) (“Rocket”) is an emerging, clinical-stage biotechnology company focused on developing first-in-class gene therapy treatment op...

Rocket Fuel

Rocket Fuel delivers a leading programmatic media-buying platform at Big Data scale that harnesses the power of artificial intelligence (AI) to improve marketing ROI in digital me...

Rocket Careers, Inc

Rocket Careers, Inc. is a direct hire service to San Francisco Bay Area biotech, pharmaceutical and medical device companies. We specialize in recruiting and placing experienced candidates in clinical...

Rocket Resources, Inc

RocketResume is a service of Rocket Resources, Inc, an Employment Information Services Company dedicated to providing job seekers the most comprehensive and up-to-date employment information availabl...

More Information about "Rocket Pharmaceuticals, Inc." on BioPortfolio

We have published hundreds of Rocket Pharmaceuticals, Inc. news stories on BioPortfolio along with dozens of Rocket Pharmaceuticals, Inc. Clinical Trials and PubMed Articles about Rocket Pharmaceuticals, Inc. for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Rocket Pharmaceuticals, Inc. Companies in our database. You can also find out about relevant Rocket Pharmaceuticals, Inc. Drugs and Medications on this site too.

Advertisement
Quick Search
Advertisement
Advertisement

 

Relevant Topics

Biotechnology - Biotech
"using living things to create products or to do tasks for humans" About Biotechnology - Biotech Biotechnology is the practice of using plants, animals and micro-organisms such as bacteria, as well as biological processes - such as the ripen...

Gene Therapy
Gene therapy is the use of DNA as a pharmaceutical agent to treat disease. It derives its name from the idea that DNA can be used to supplement or alter genes within an individual's cells as a therapy to treat disease. The most common form of gene th...

Biological Therapy
Biological therapy involves the use of living organisms, substances derived from living organisms, or laboratory-produced versions of such substances to treat disease. Some biological therapies for cancer use vaccines or bacteria to stimulate the body&rs...


Corporate Database Quicklinks



Searches Linking to this Company Record