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Rocket Pharmaceuticals, Inc. Company Profile

00:16 EST 21st January 2019 | BioPortfolio

Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) (“Rocket”) is an emerging, clinical-stage biotechnology company focused on developing first-in-class gene therapy treatment options for rare, undertreated diseases. Rocket’s multi-platform development approach applies the well-established lentiviral vector (LVV) and adeno-associated viral vector (AAV) gene therapy platforms. Rocket's lead clinical program is a LVV-based gene therapy for the treatment of Fanconi Anemia (FA), a difficult to treat genetic disease that leads to bone marrow failure and potentially cancer. Preclinical studies of additional bone marrow-derived disorders are ongoing and target Pyruvate Kinase Deficiency (PKD), Leukocyte Adhesion Deficiency-I (LAD-I) and Infantile Malignant Osteopetrosis (IMO). Rocket is also developing an AAV-based gene therapy program for an undisclosed rare pediatric disease.


News Articles [346 Associated News Articles listed on BioPortfolio]

Rocket Pharma nets $68.5mm via FOPO

Gene therapies developer Rocket Pharmaceuticals Inc. netted $68.5mm via a follow-on public offering of 5.5mm common shares at $13.25. The company will use the proceeds for ongoing development of its r...

Rocket Pharmaceuticals Announces Clearance of IND for RP-L201 Gene Therapy

Rocket Pharmaceuticals (Nasdaq:RCKT) a leading U.S.-based multi-platform gene therapy company, announces the clearance of the Company’s Investigational New Drug (IND) application by the U.S. Food a...

Rocket, Inotek reverse merge

Public Inotek Pharmaceuticals Corp. entered into a definitive agreement to merge with closely held Rocket Pharmaceuticals Inc. in a stock swap.

RMAT, fast-track statuses given to Rocket's Fanconi anemia drug

Rocket Pharmaceuticals' RP-L102, a lentiviral vector-based gene therapy that is being developed to treat patients with Fancon -More- 

Rocket's IND for leukocyte adhesion deficiency-I drug OK'd by FDA

Rocket Pharmaceuticals' investigational new drug application for its RP-L201 gene therapy received approval from the FDA, all -More- 

Rocket Pharmaceuticals Receives FDA Drug Clearance

The company’s drug, PR-L201, is in development to treat Leukocyte Adhesion Deficiency-I, a rare pediatric disease. The post Rocket Pharmaceuticals Receives FDA Drug Clearance appeared first on Inves...

Rocket Pharma nets $59.5mm via FOPO

Rocket Pharmaceuticals Inc. (focused on developing gene therapies for rare pediatric diseases) netted $59.5mm through the follow-on sale of 4.08mm common shares (including full exercise of the overall...

Rocket Pharma provides update on Fanconi anemia study in Spain

Rocket Pharmaceuticals unveiled updated long-term results from a Phase I/II study being conducted in Spain to assess its gene -More- 

Drugs and Medications [0 Results]

None

PubMed Articles [143 Associated PubMed Articles listed on BioPortfolio]

Swimming activity in zebrafish larvae exposed to veterinary antiparasitic pharmaceuticals.

Veterinary antiparasitic pharmaceuticals have been detected in surface waters and several of these pharmaceuticals act on the nervous system on the target organisms implying that neurological effects ...

In artificial roost comparison, bats show preference for rocket box style.

Understanding microhabitat preferences of animals is critical for effective conservation, especially for temperate-zone bats, which receive fitness benefits from selecting optimal roost microhabitats....

Insight into the distribution of pharmaceuticals in soil-water-plant systems.

Pharmaceuticals in agricultural soils originating from irrigation with treated wastewater and land-applied biosolids can enter field crops. However, little is known about the role of pore water in pla...

Chiral pharmaceuticals: Environment sources, potential human health impacts, remediation technologies and future perspective.

Chiral pharmaceuticals (CPs), including non-steroid anti-inflammatory drugs (NSAIDs), β-blockers and some herbicide and pesticides, are widely used in aquaculture, clinical treatment and many other f...

Assessment of 83 pharmaceuticals in WWTP influent and effluent samples by UHPLC-MS/MS: Hourly variation.

The removal efficiency of pharmaceuticals in wastewater treatment plants (WWTPs) is variable and some of these compounds pass these plants almost intact and others presenting a removal efficiency clos...

Clinical Trials [239 Associated Clinical Trials listed on BioPortfolio]

Rocket® Pleural Catheters: QOL, Feasibility and Satisfaction in Recurrent MPE Patients

This study will take place in Ottawa, Ontario, and will include 100 patients who are receiving tunnelled pleural catheters to treat their symptoms of MPE. The aim of this study is to evalu...

Quality of Life of Patients Who Have Rocket Indwelling Pleural Catheter Drainage or Repeated Large Volume Paracentesis

Ascites (accumulation of fluid in the abdominal cavity) is a common problem which can lead to distressing symptoms. When caused by cancer, management options are chemotherapy, diuretics an...

Bioequivalence Study of Torrent Pharmaceuticals Ltd's Nebivolol 20 mg Tablet

Subjects to compare the single dose bioavailability of Torrent's Nebivolol Tablets 20 mg and Bystolic®20 mg Tablets of Forest Pharmaceuticals Inc., USA. Dosing periods of studies were sep...

Bioequivalence Study of Torrent Pharmaceuticals's Ltd's Nebivolol 20 mg Tablet

Subjects to compare the single dose bioavailability of Torrent's Nebivolol Tablets 20 mg and Bystolic 20 mg Tablets of Forest Pharmaceuticals Inc., USA. Dosing periods of studies were sepa...

Study Comparing Citalopram Hydrobromide Tablets 40 mg (Torrent Pharmaceuticals Ltd) and RLD Tablets 40 mg (Manufactured By Forest Pharmaceuticals Inc, Missouri) in 24+2 Normal Healthy Male Subjects in Fed Condition

- Objective: - The objective of this study is to compare the rate and extent of absorption of the Test Product, Citalopram Hydrobromide 40 mg (Torrent Pharmaceutical Li...

Companies [1351 Associated Companies listed on BioPortfolio]

Rocket Pharmaceuticals, Ltd.

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) (“Rocket”) is an emerging, clinical-stage biotechnology company focused on developing first-in-class gene therapy treatment o...

Rocket Pharmaceuticals, Inc.

Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT) (“Rocket”) is an emerging, clinical-stage biotechnology company focused on developing first-in-class gene therapy treatment op...

Rocket Fuel

Rocket Fuel delivers a leading programmatic media-buying platform at Big Data scale that harnesses the power of artificial intelligence (AI) to improve marketing ROI in digital me...

Rocket Careers, Inc

Rocket Careers, Inc. is a direct hire service to San Francisco Bay Area biotech, pharmaceutical and medical device companies. We specialize in recruiting and placing experienced candidates in clinical...

Rocket Resources, Inc

RocketResume is a service of Rocket Resources, Inc, an Employment Information Services Company dedicated to providing job seekers the most comprehensive and up-to-date employment information availabl...

More Information about "Rocket Pharmaceuticals, Inc." on BioPortfolio

We have published hundreds of Rocket Pharmaceuticals, Inc. news stories on BioPortfolio along with dozens of Rocket Pharmaceuticals, Inc. Clinical Trials and PubMed Articles about Rocket Pharmaceuticals, Inc. for you to read. In addition to the medical data, news and clinical trials, BioPortfolio also has a large collection of Rocket Pharmaceuticals, Inc. Companies in our database. You can also find out about relevant Rocket Pharmaceuticals, Inc. Drugs and Medications on this site too.

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Relevant Topics

Biotechnology - Biotech
"using living things to create products or to do tasks for humans" About Biotechnology - Biotech Biotechnology is the practice of using plants, animals and micro-organisms such as bacteria, as well as biological processes - such as the ripen...

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