Marketing authorization application for Luxturna filed

10:30 EDT 1 Aug 2017 | Healio

Spark Therapeutics has submitted a marketing authorization application to the European Medicines Agency for Luxturna, its one-time gene therapy for the treatment of vision loss, according to a company press release.Luxturna, the proposed trade name for voretigene neparvovec, would treat vision loss caused by biallelic RPE65 gene mutations in Leber congenital amaurosis or retinitis pigmentosa, the release said.

Original Article: Marketing authorization application for Luxturna filed


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