Track topics on Twitter Track topics that are important to you
The first gene therapy to treat a rare blood disorder is one step closer to approval following a positive regulatory action taken by European officials.
Original Article: First gene therapy to treat rare blood disease nears European approvalNEXT ARTICLE
Gene therapy is the use of DNA as a pharmaceutical agent to treat disease. It derives its name from the idea that DNA can be used to supplement or alter genes within an individual's cells as a therapy to treat disease. The most common form of gene th...