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Accelerating the Science of Sickle Cell Disease Therapies—Is a Cure Possible?

20:00 EDT 7 Aug 2019 | JAMA

This Viewpoint reviews the molecular basis of sickle cell disease (SCD), the history of treatments for the disease, and recent progress toward curative therapies including HSCT and gene therapy and editing, emphasizing that research and innovation needs to take into account patient priorities and perspectives given the history of research mistreatment of minority groups most affected by SCD.

Original Article: Accelerating the Science of Sickle Cell Disease Therapies—Is a Cure Possible?

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