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(MedPage Today) -- Neurologic scores stabilized, seizures diminished with tailored antisense oligonucleotide therapy
Original Article: Mila's N-of-1 Trial Detailed in NEJMNEXT ARTICLE
Most human diseases are caused by production of abnormal proteins or malfunctioning proteins. Antisense therapy involves inhibiting production of these proteins. When a gene is known to cause a specific disease and the genetic sequence ...