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Promising Results Reported in Tay-Sachs Gene Therapy Trial

08:00 EDT 29 Oct 2019 | Genetic Engineering News

Terence R. Flotte, MD, executive deputy chancellor, provost, and dean of the University of Massachusetts School of Medicine, presented the first signs of clinical benefit in an early-stage gene therapy trial for Tay-Sachs disease on two infants. Flotte said there are early signs that the therapy, which in 2018 was licensed to Axovant Gene Therapies, has the potential to modify the rate of disease progression.

The post Promising Results Reported in Tay-Sachs Gene Therapy Trial appeared first on GEN - Genetic Engineering and Biotechnology News.

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