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Choroideremia Gene Therapy Phase 2 Clinical Trial: 24-Month Results.

08:00 EDT 18th September 2018 | BioPortfolio

Summary of "Choroideremia Gene Therapy Phase 2 Clinical Trial: 24-Month Results."

To report the final results of a phase 2 high-dose gene therapy clinical trial in choroideremia.

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Journal Details

This article was published in the following journal.

Name: American journal of ophthalmology
ISSN: 1879-1891
Pages:

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Clinical study in which a prospectively planned opportunity is included to modify trial designs and hypotheses based on analysis of data from subjects in the study.

Work that is the report of a pre-planned, usually controlled, clinical study of the safety and efficacy of diagnostic, therapeutic, or prophylactic drugs, devices, or techniques based on a small number of healthy persons and conducted over the period of about a year in either the United States or a foreign country.

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